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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,243 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Enrolling by Invitation

Post-marketing Surveillance (Special Use-results Surveillance) on Treatment With Alhemo

NCT06831734

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +9 more
Locations
  • Chiba university hospital_Pediatrics Chiba, Japan
  • National Hospital Organization Awara Hospital_Hematology and Oncology Fukui, Japan
  • Hoshi General Hospital_Pediatrics Fukushima, Japan
  • Hyogo Prefectural Amagasaki General Medical Center_Haematology Hyōgo, Japan
View all 23 locations
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Enrolling by Invitation

Post-Marketing Surveillance (All Case Surveillance) on Treatment With Alhemo® in Patients With Haemophilia A or Haemophilia B With Inhibitors

NCT06285071

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +10 more
Locations
  • Novo Nordisk Investigational Site Toshima City, Tokyo, Japan
  • Mutsu general hospital_Pediatrics Aomori, Japan
  • Kyushu university hospital_Pediatrics Fukuoka, Japan
  • Sapporo Tokushukai Hospital_Pediatrics Hokkaido, Japan
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Enrolling by Invitation

A Study Following Males With Haemophilia B on Prophylaxis With Refixia/REBINYN

NCT03745924

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
Locations
  • AKH - Klin. Abt. f. Haematologie u. Haemostaseologie Vienna, Austria
  • Cliniques universitaires Saint-Luc - Service Hématologie Brussels, Belgium
  • UZ Antwerpen - UZA - Kinderhemato-Oncologie Edegem, Belgium
  • UZ Leuven - Hart en Vaatziekten Leuven, Belgium
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Enrolling by Invitation

An Extension Study of the Long-Term Safety, Tolerability, and Efficacy of Tividenofusp Alfa (DNL310) in Participants With Mucopolysaccharidosis Type II (MPS II) From Study DNLI-E-0002 or Study DNLI-E-0007

NCT06075537

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Ann and Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Hackensack University Medical Center Hackensack, New Jersey, United States
  • UNC Children's Research Institute Chapel Hill, North Carolina, United States
View all 29 locations
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Enrolling by Invitation

An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy

NCT06270719

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital Los Angeles - PIN Los Angeles, California, United States
  • University of Colorado - PPDS Aurora, Colorado, United States
  • Connecticut Children's Medical Center - Hartford Hartford, Connecticut, United States
View all 25 locations
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