NCT04528355
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
Clinical trial condition
Wiskott-Aldrich Syndrome
Explore clinical trials studying Wiskott-Aldrich Syndrome. Study availability and eligibility vary by location and protocol.
31 public trials
2 recruiting studies
Wiskott-Aldrich Syndrome trial results
NCT01962415
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
Enrolling by invitation
Analysis of the Therapeutic and Clinical Profile of Cannabinoid Treatments: A Real-World Study
NCT07362407
- Conditions
- Anxiety Disorders, Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, +34 more
- Locations
-
- Universidade Federal de Santa Catarina (UFSC), Centro de Ciências Biológicas (CCB), Campus Universitário, Trindade, Florianópolis - SC. Florianópolis, Santa Catarina, Brazil
Enrolling by invitation
Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases
NCT01852370
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Chronic Disease, +35 more
- Locations
-
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
Active, not recruiting
Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune Deficiencies
NCT01652092
- Conditions
- Albinism, Bare Lymphocyte Syndrome, Blood Coagulation Disorders, +54 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Active, not recruiting
Immune Disorder HSCT Protocol
NCT01821781
- Conditions
- 22q11 Deletion Syndrome, Abnormalities, Multiple, Albinism, +66 more
- Locations
-
- Washington University St Louis, Missouri, United States
Active, not recruiting
A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome
NCT03837483
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Children's Healthcare of Atlanta, Inc Atlanta, Georgia, United States
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
Active, not recruiting
Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome
NCT02333760
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Hopital Necker - Enfants Malades Paris, France
- UCL Institute of Child Health London, United Kingdom
NCT01410825
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Children's Hospital Boston Boston, Massachusetts, United States
Completed
Baby Detect : Genomic Newborn Screening
NCT05687474
- Conditions
- 3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
- Locations
-
- CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium