Active, Not Recruiting
Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome
NCT02333760
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Hopital Necker - Enfants Malades Paris, France
- UCL Institute of Child Health London, United Kingdom