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Clinical trial condition

Urea Cycle Disorders, Inborn

Explore clinical trials studying Urea Cycle Disorders, Inborn. Study availability and eligibility vary by location and protocol.

50 public trials 11 recruiting studies
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Urea Cycle Disorders, Inborn trial results

Completed

Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset Ornithine Transcarbamylase (OTC) Deficiency

NCT02991144

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
Locations
  • The Children's Hospital Colorado Aurora, Colorado, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
  • Icahn School of Medicine at Mount Sinai New York, United States
  • University Hospital Cleveland Medical Center/Case Western Reserve University Cleveland, Ohio, United States
View Trial Details
Completed

PCORI Urea Cycle Disorder Study

NCT02740153

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • Childrens Research Institute Washington D.C., District of Columbia, United States
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Completed

Safety Study of HepaStem for the Treatment of Urea Cycle Disorders (UCD) and Crigler-Najjar Syndrome (CN)

NCT01765283

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
Locations
  • Saint Luc University Hospital Brussels, Belgium
  • Universitair Ziekenhuis (UZ) Antwerpen Edegem, Belgium
  • CHU Bicêtre Le Kremlin-Bicêtre, France
  • Hôpital Jeanne de Flandre, CHRU Lille Lille, France
View Trial Details
Completed

Study to Evaluate the Efficacy of HepaStem in Urea Cycle Disorders Paediatric Patients (HEP002)

NCT02489292

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • Cliniques Universitaires Saint-Luc Brussels, Belgium
  • Hôpital Jeanne de Flandre, CHRU Lille Lille, France
  • Instytut - Pomnik Centrum Zdrowia Dziecka Warsaw, Poland
  • Hospital Materno Infatil de Badajoz Badajoz, Spain
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