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Clinical trial condition

Urea Cycle Disorders, Inborn

Explore clinical trials studying Urea Cycle Disorders, Inborn. Study availability and eligibility vary by location and protocol.

49 public trials 10 recruiting studies
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Urea Cycle Disorders, Inborn trial results

Completed

A Study of the Safety, Efficacy and Pharmacokinetics of Glycerol Phenylbutyrate in Pediatric Subjects Under 2 Years of Age With Urea Cycle Disorders

NCT02246218

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
Locations
  • Kaiser Permanente Regional Metabolic Center Los Angeles, California, United States
  • Stanford Center for Clinical & Translational Research & Education Palo Alto, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • Shands at University of Florida Gainesville, Florida, United States
View all 17 locations
View Trial Details
Completed

Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset Ornithine Transcarbamylase (OTC) Deficiency

NCT02991144

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
Locations
  • The Children's Hospital Colorado Aurora, Colorado, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
  • Icahn School of Medicine at Mount Sinai New York, United States
  • University Hospital Cleveland Medical Center/Case Western Reserve University Cleveland, Ohio, United States
View Trial Details
Completed

PCORI Urea Cycle Disorder Study

NCT02740153

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • Childrens Research Institute Washington D.C., District of Columbia, United States
View Trial Details

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