Not Yet Recruiting
A Phase I/II Open-label Safety and Efficacy Study of LNP.UCD.ABE in Patients With Urea Cycle Disorders.
NCT07667387
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +11 more
- Locations
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- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States