Active, Not Recruiting
Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)
NCT06100276
- Conditions
- Amyotrophic Lateral Sclerosis, Central Nervous System Diseases, Metabolic Diseases, +8 more
- Locations
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- Barrow Neurological Institute Phoenix, Arizona, United States
- University of California Irvine Irvine, California, United States
- California Pacific Medical Center San Francisco, California, United States
- Mayo Clinic Florida Jacksonville, Florida, United States