Active, Not Recruiting
A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy
NCT06907875
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- David Geffen School of Medicine at University of California, Los Angeles Los Angeles, California, United States
- Rare Disease Research Atlanta, Georgia, United States
- Kennedy Krieger Institute, Center for Genetic Muscle Disorders Baltimore, Maryland, United States
- University of Massachusetts Chan Medical School Worcester, Massachusetts, United States