NCT00102453
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
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- Children's National Medical Center Washington D.C., District of Columbia, United States
- Mayo Clinic Rochester, Minnesota, United States
- Washington University at St. Louis St Louis, Missouri, United States
- Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States