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Clinical trial condition

Muscular Disorders, Atrophic

Explore clinical trials studying Muscular Disorders, Atrophic. Study availability and eligibility vary by location and protocol.

622 public trials 123 recruiting studies
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Muscular Disorders, Atrophic trial results

Completed

Study of AOC 1044 in Healthy Adult Volunteers and Participants With Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 Skipping

NCT05670730

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Exon 44, +9 more
Locations
  • Arkansas Children's Little Rock, Arkansas, United States
  • UCSD La Jolla, California, United States
  • Stanford University Palo Alto, California, United States
  • Rare Disease Research - Atlanta Atlanta, Georgia, United States
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Completed

A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)

NCT05096221

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Little Rock, Arkansas, United States
  • UC San Diego Altman Clinical and Translational Research Institute La Jolla, California, United States
  • UCLA Medical Center Los Angeles, California, United States
  • Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
View all 42 locations
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Completed

Safety and Efficacy of Pitolisant on Excessive Daytime Sleepiness and Other Non-Muscular Symptoms in Patients With Myotonic Dystrophy Type 1

NCT04886518

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disorders of Excessive Somnolence, Dyssomnias, +16 more
Locations
  • UCI Center for Clinical Research Irvine, California, United States
  • University of Colorado School of Medicine Aurora, Colorado, United States
  • University of South Florida Tampa, Florida, United States
  • Rare Disease Research Atlanta, Georgia, United States
View all 13 locations
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