NCT00744692
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +43 more
- Locations
-
- Duke University Medical Center Pediatric Blood and Marrow Transplant Program Durham, North Carolina, United States
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
81 public trials
12 recruiting studies
Lysosomal Storage Diseases trial results
NCT01275066
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Oakland, California, United States
- Wilmington, Delaware, United States
- Washington D.C., District of Columbia, United States
- Chicago, Illinois, United States
NCT00884949
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Birmingham, United Kingdom
- London, United Kingdom
- Manchester, United Kingdom
NCT02082327
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- PRA International Groningen, Netherlands
Completed
Migalastat Food Effect Study
NCT01489995
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- GSK Investigational Site Austin, Texas, United States
NCT01432561
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Genetic Diseases, Inborn, +5 more
- Locations
-
- University of California, San Diego Center for Clinical Research Services (CCR) La Jolla, California, United States
NCT00351156
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
- University of California - San Francisco San Francisco, California, United States
- University Research Foundation for Lysosomal Storage Diseases, Inc. Coral Springs, Florida, United States
- Emory University Lysosomal Storage Disease Center Decatur, Georgia, United States
- National Institute of Neurological Disorders and Stroke, NIH Bethesda, Maryland, United States
NCT00001780
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Demyelinating Disease, +15 more
- Locations
-
- National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States
NCT04455230
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Charité - Universitätsmedizin Berlin Berlin, Germany
- Royal Free London London, United Kingdom
Terminated
A Fabry Disease Gene Therapy Study
NCT04040049
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Kaiser Permanente Los Angeles, California, United States
- Columbia University New York, United States
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center Fairfax, Virginia, United States