- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Birmingham Children's Hospital Birmingham, United Kingdom
- Birmingham Children's Hospital NHS Foundation Trust Birmingham, United Kingdom
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
81 public trials
12 recruiting studies
Lysosomal Storage Diseases trial results
NCT01155778
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Emma Children's Hospital, Academic Medical Center Amsterdam, Netherlands
- St. Mary's Hospital Manchester, United Kingdom
NCT02055118
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Children's Hospital and Research Center at Oakland Oakland, California, United States
- Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina Chapel Hill, North Carolina, United States
- Women's and Children's Hospital, 72 King William Road North Adelaide, Australia
NCT00630747
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- St. Joseph's Hospital Phoenix, Arizona, United States
- Pediatric Clinical Research Center, Children's Hospital Oakland Oakland, California, United States
- The Children's Hospital Denver, Colorado, United States
- Harbin Clinic Rome, Georgia, United States
NCT00607386
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
- Instytut Pomnik Centrum Zdrowia Dziecka, Klinika Chorob Metaboliczynch, Endokrynologii i Diabetologii Warsaw, Poland
- National Taiwan University Hospital, Dept. of Pediatrics and Medical Genetics Taipei, Taiwan
NCT02060526
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +18 more
- Locations
-
- Los Angeles Biomedical Research Torrance, California, United States
- University of Minnesota Department of Pediatrics Minneapolis, Minnesota, United States
- University of North Carolina Chapel Hill, North Carolina, United States
- Hospital Universitario Austral A Unidad de Investigacion Buenos Aires, Argentina
NCT00882921
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Children's Hospital & Research Center Oakland Oakland, California, United States
- Children's Hospitals and Clinics of Minnesota, Division of Genetics Minneapolis, Minnesota, United States
- Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
- Birmingham Children's Hospital Birmingham, United Kingdom
NCT02416661
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- University Hospital Center Mother Teresa Tirana, Albania
- Aristotle University of Thessaloniki, Ippokration General Hospital Thessaloniki, Greece
- Centre for Human Genetics Bangalore, India
- Shaare Zedek Medical Center Jerusalem, Israel
Completed
Diet and Exercise in Pompe Disease
NCT02363153
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- University of Florida Clinical Research Center Gainesville, Florida, United States
NCT01757184
- Conditions
- Cholesterol Ester Storage Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
-
- Tucson, Arizona, United States
- Palo Alto, California, United States
- San Francisco, California, United States
- Wilmington, Delaware, United States