NCT01560182
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
77 public trials
13 recruiting studies
Lysosomal Storage Diseases trial results
NCT04041102
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Hospital de Clínicas de Porto Alegre Porto Alegre, Brazil
- Montreal Children's Hospital Research Institute - McGill University Montreal, Quebec, Canada
NCT05109793
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Mayo Clinic Rochester Rochester, Minnesota, United States
- Hospital Pequeno Principe Curitiba, Brazil
- Hospital de Clinicas de Porto Alegre Porto Alegre, Brazil
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Ann & Robert H Lurie Childrens Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Legacy Emanuel Hospital Portland, Oregon, United States
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
NCT06475404
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +19 more
- Locations
-
- State budgetary healthcare institution of the city of Moscow "City Clinic No. 2 of the Moscow Health Department" Moscow, Russia
Completed
A Study of Potential Treatment-Responsive Biomarkers and Clinical Outcomes in Hunter Syndrome
NCT04007536
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- UNC Children's Research Institute Chapel Hill, North Carolina, United States
- UPMC | Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Erasmus Medical Center Rotterdam, South Holland, Netherlands
NCT04455230
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Charité - Universitätsmedizin Berlin Berlin, Germany
- Royal Free London London, United Kingdom
NCT01891422
- Conditions
- Alpha Mannosidosis, Aspartylglucosaminuria, Beta Mannosidosis, +29 more
- Locations
-
- Greenwood Genetic Center North Charleston, South Carolina, United States
NCT04310163
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- Casimir Trials Plymouth, Massachusetts, United States
NCT03893240
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +17 more
- Locations
-
- Barrow Neurological Institute Phoenix, Arizona, United States
- University of California Irvine Health Orange, California, United States
- University of Kansas Medical Center Kansas City, Kansas, United States
- University of Minnesota Medical School Minneapolis, Minnesota, United States