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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
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Lysosomal Storage Diseases trial results

Completed

BMN 110 Phase 3B in Australian Patients

NCT01966029

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children's Hospital at Westmead Westmead, New South Wales, Australia
  • Lady Cilento Children's Hospital (previous: Royal Children's Hospital) Brisbane, Queensland, Australia
  • Murdoch Childrens Research Institute and Royal Children's Hospital Melbourne, Victoria, Australia
  • Princess Margaret Hospital for Children Perth, Western Australia, Australia
View Trial Details
Completed

Longitudinal Studies of Brain Structure and Function in MPS Disorders

NCT01870375

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +31 more
Locations
  • Oakland Children's Hospital Oakland, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • New York University New York, United States
  • Hospital for Sick Children Toronto, Ontario, Canada
View Trial Details
Completed

Stem Cell Transplant w/Laronidase for Hurler

NCT00176891

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
View Trial Details

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