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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies

Lysosomal Storage Diseases trial results

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Investigational Site Number 840002 Atlanta, Georgia, United States
  • Investigational Site Number 840003 Cincinnati, Ohio, United States
  • Investigational Site Number 840001 Fairfax, Virginia, United States
  • Investigational Site Number 250001 Garches, France
Conditions
Alpha-Mannosidosis, Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +7 more
Locations
  • National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • Hôpital Femme-Mère-Enfant Bron, France
  • Villa Metabolica Mainz, Germany
  • Centro Hospitalar S. João Porto, Portugal
  • Royal Free Hospital London, United Kingdom

NCT01920828

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more
Locations
  • Oregon Health and Science University Portland, Oregon, United States