NCT05798416
- Conditions
- Acute Mountain Sickness, Altitude Sickness, Carbohydrate Metabolism, Inborn Errors, +18 more
- Locations
-
- The First Affiliated Hospital of Guangzhou Medical University Guangzhou, Guangdong, China
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
710 public trials
130 recruiting studies
Lysosomal Storage Diseases trial results
Completed
A Multicenter Extension Study of Taliglucerase Alfa in Adult Subjects With Gaucher Disease
NCT01422187
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
Not specified
NCT02798458
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Massachusetts General Hospital Boston, Massachusetts, United States
Completed
Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients.
NCT01898364
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +15 more
- Locations
-
- Investigational Site Number 840006 Phoenix, Arizona, United States
- Investigational Site Number 840010 Jacksonville, Florida, United States
- Investigational Site Number 840001 Kansas City, Kansas, United States
- Investigational Site Number 840008 St Louis, Missouri, United States
NCT02746718
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- CHU d'Angers Angers, France
- Centre hospitalier d'Argenteuil Argenteuil, France
- CHU de Brest Brest, France
- CH d'Escartons Briançon, France
NCT05186324
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- #02 Birmingham, Alabama, United States
- #03 Atlanta, Georgia, United States
- #04 Iowa City, Iowa, United States
- #11 Grand Rapids, Michigan, United States
NCT03053089
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- HCPA - Hospital das Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
Completed
Extension Study Evaluating Long Term Safety and Activity of AGT-181 in Children With MPS I
NCT03071341
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- HCPA - Hospital das Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
NCT02534844
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +34 more
- Locations
-
- University of Alabama at Birmingham Birmingham, Alabama, United States
- Children's Hospital of Orange County Orange, California, United States
- University of California San Francisco San Francisco, California, United States
- University of Colorado Denver Aurora, Colorado, United States
Completed
Safety and Dose Ranging Study of Insulin Receptor MAb-IDUA Fusion Protein in Patients With MPS I
NCT02371226
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- Children's Hospital Oakland Oakland, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Emory Healthcare Decatur, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States