NCT00004378
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +47 more
- Locations
-
- University of California Los Angeles Medical Center Los Angeles, California, United States
Clinical trial condition
Leukodystrophy, Metachromatic
Explore clinical trials studying Leukodystrophy, Metachromatic. Study availability and eligibility vary by location and protocol.
34 public trials
9 recruiting studies
Leukodystrophy, Metachromatic trial results
Active, Not Recruiting
Early Check: Expanded Screening in Newborns
NCT03655223
- Conditions
- 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
- Locations
-
- RTI International Research Triangle Park, North Carolina, United States
Active, Not Recruiting
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Active, Not Recruiting
OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)
NCT04283227
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
Related conditions
- Brain Diseases (34)
- Brain Diseases, Metabolic (34)
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (34)
- Hereditary Central Nervous System Demyelinating Diseases (34)
- Lipid Metabolism Disorders (34)
- Lipid Metabolism, Inborn Errors (34)
- Lipidoses (34)
- Lysosomal Storage Diseases, Nervous System (34)