NCT03771898
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- Los Angeles Biomedical Research Institute at Harbor-UCLA Torrance, California, United States
- Childrens Hospital Colorado Aurora, Colorado, United States
- Rare Disease Research, LLC Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States