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Clinical trial condition

Lipid Metabolism, Inborn Errors

Explore clinical trials studying Lipid Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

836 public trials 154 recruiting studies
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Lipid Metabolism, Inborn Errors trial results

Recruiting

Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy

NCT07220785

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Generalized Lipodystrophy, Genetic Diseases, Inborn, +12 more
Locations
  • University of Michigan Ann Arbor, Michigan, United States
  • UT Southwestern Medical Center Dallas, Texas, United States
  • Assistance Publique-Hopitaux de Paris (AP-HP) Paris, France
  • Hopital Universitaire Robert-Debre Paris, France
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Recruiting

Study of ARO-DIMERPA in Adult Participants With Mixed Hyperlipidemia

NCT07223658

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Genetic Diseases, Inborn, +9 more
Locations
  • Research Site 7 Charlestown, New South Wales, Australia
  • Research Site 5 Morayfield, Queensland, Australia
  • Research Site 8 East Melbourne, Victoria, Australia
  • Research Site 4 Melbourne, Victoria, Australia
View all 17 locations
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Recruiting

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC)

NCT07082725

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • UCSF Children's Hospital and Research Center at Oakland Oakland, California, United States
  • University of Minnesota Medical School Minneapolis, Minnesota, United States
  • Mayo Clinic Children's Center - PIN Rochester, Minnesota, United States
  • Children's Medical Center Dallas Dallas, Texas, United States
View all 34 locations
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Recruiting

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis

NCT07054515

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +25 more
Locations
  • UCSF Children's Hospital and Research Center at Oakland Oakland, California, United States
  • University of Minnesota Medical School Minneapolis, Minnesota, United States
  • Mayo Clinic Childrens Center - PIN Rochester, Minnesota, United States
  • Children's Medical Center Dallas Dallas, Texas, United States
View all 38 locations
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Recruiting

A Gaucher Disease Gene Therapy Trial With FLT201

NCT07223944

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Kaiser Permanente - CA Los Angeles, California, United States
  • UCLA Health Los Angeles, California, United States
  • University of California, San Francisco (UCSF) San Francisco, California, United States
  • University of Colorado Anschutz Aurora, Colorado, United States
View all 33 locations
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