Skip to main content
OpenTrials

Clinical trial condition

Lipid Metabolism, Inborn Errors

Explore clinical trials studying Lipid Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

841 public trials 150 recruiting studies
Refine in advanced search Browse all conditions

Lipid Metabolism, Inborn Errors trial results

Recruiting

A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)

NCT06192576

Conditions
Acid Sphingomyelinase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +19 more
Locations
  • Ann and Robert H Lurie Children's Hospital of Chicago- Site Number: 001002 Chicago, Illinois, United States
  • Children's Hospital Medical Center- Site Number: 001003 Cincinnati, Ohio, United States
  • Pulse InfoFrame US Inc.- Site Number: 001001 Philadelphia, Pennsylvania, United States
  • Dell Children's Medical Center- Site Number : 1001-2 Austin, Texas, United States
View Trial Details
Recruiting

Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy

NCT07220785

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Generalized Lipodystrophy, Genetic Diseases, Inborn, +12 more
Locations
  • University of Michigan Ann Arbor, Michigan, United States
  • UT Southwestern Medical Center Dallas, Texas, United States
  • Assistance Publique-Hopitaux de Paris (AP-HP) Paris, France
  • Hopital Universitaire Robert-Debre Paris, France
View Trial Details
Recruiting

A Study of Patients With Fabry Disease (US Specific)

NCT06906367

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • UAB Nephrology Research Clinic at Paula Building Birmingham, Alabama, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Emory Genetics Atlanta, Georgia, United States
  • Washington University School of Medicine St Louis, Missouri, United States
View Trial Details
Recruiting

A Gaucher Disease Gene Therapy Trial With FLT201

NCT07223944

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Kaiser Permanente - CA Los Angeles, California, United States
  • UCLA Health Los Angeles, California, United States
  • University of California, San Francisco (UCSF) San Francisco, California, United States
  • University of Colorado Anschutz Aurora, Colorado, United States
View all 33 locations
View Trial Details

Related conditions