- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +17 more
- Locations
-
- National Cancer Institute (NCI) Bethesda, Maryland, United States
Clinical trial condition
Heredodegenerative Disorders, Nervous System
Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.
1,879 public trials
409 recruiting studies
Heredodegenerative Disorders, Nervous System trial results
Completed
ERG/5-HTP in Fragile X Syndrome (FXS)
NCT05030129
- Conditions
- Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
-
- Rush University Medical Center Chicago, Illinois, United States
Completed
Single and Multiple Ascending Dose Study Assessing the Safety, Tolerability, PK and PD of AG10
NCT03294707
- Conditions
- Amyloid Cardiomyopathy, Transthyretin-Related, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +13 more
- Locations
-
- Celerion Tempe, Arizona, United States
NCT05890833
- Conditions
- Autoimmune Diseases, Autoimmune Diseases of the Nervous System, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +26 more
- Locations
-
- Marko Mijic München, Bavaria, Germany
Completed
Tourette Syndrome Deep Brain Stimulation
NCT02056873
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +10 more
- Locations
-
- University of Florida Gainesville, Florida, United States
NCT00052143
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +13 more
- Locations
-
- University of Alabama Birmingham, Alabama, United States
- Mayo Clinic Arizona Phoenix, Arizona, United States
- University of California at San Diego La Jolla, California, United States
- UCLA School of Medicine Los Angeles, California, United States
NCT06576388
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
-
- Hangzhou Jiayin Biotechnology Co., Ltd Hangzhou, Zhejiang, China
NCT05693376
- Conditions
- Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +19 more
- Locations
-
- University Hospital Essen Essen, North Rhine-Westphalia, Germany
NCT02849457
- Conditions
- Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +13 more
- Locations
-
- University of Alabama at Birmingham Birmingham, Alabama, United States
- University of California, Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
NCT01445314
- Conditions
- Behavior, Brain Diseases, Brain Neoplasms, +23 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States