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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,879 public trials 409 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Completed

Study to Evaluate QR-110 in Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene

NCT03140969

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +14 more
Locations
  • University of Iowa Iowa City, Iowa, United States
  • Scheie Eye Institute, University of Pennsylvania Philadelphia, Pennsylvania, United States
  • Ghent University Hospital and Ghent University Ghent, Belgium
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Completed

Safety and Efficacy of Intravenous OAV101 (AVXS-101) in Pediatric Patients With Spinal Muscular Atrophy (SMA)

NCT04851873

Conditions
Atrophy, Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, +19 more
Locations
  • Novartis Investigative Site Boston, Massachusetts, United States
  • Novartis Investigative Site St Louis, Missouri, United States
  • Novartis Investigative Site Randwick, New South Wales, Australia
  • Novartis Investigative Site Leuven, Belgium
View all 13 locations
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Completed

Safety and Efficacy of Intravenous OAV101 (AVXS-101) in Pediatric Patients With Spinal Muscular Atrophy (SMA) (OFELIA)

NCT05073133

Conditions
Atrophy, Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, +18 more
Locations
  • Novartis Investigative Site CABA, Buenos Aires, Argentina
  • Novartis Investigative Site Buenos Aires, Argentina
  • Novartis Investigative Site Belo Horizonte, Minas Gerais, Brazil
  • Novartis Investigative Site Porto Alegre, Rio Grande do Sul, Brazil
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Completed

Berzosertib + Topotecan in Relapsed Platinum-Resistant Small-Cell Lung Cancer (DDRiver SCLC 250)

NCT04768296

Conditions
Bronchial Neoplasms, Carcinoma, Bronchogenic, Congenital Abnormalities, +19 more
Locations
  • Providence Medical Foundation Santa Rosa, California, United States
  • St Joseph Heritage Healthcare Santa Rosa, California, United States
  • Cotton-O'Neil Clinical Research Center, Hematology and Oncology Topeka, Kansas, United States
  • National Cancer Institute Bethesda, Maryland, United States
View all 51 locations
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