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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Recruiting

A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's Ataxia

NCT06953583

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +11 more
Locations
  • UCLA Neurology Outpatient Clinic at Westwood Los Angeles, California, United States
  • Norman Fixel Institute for Neurological Diseases UF Health Gainesville, Florida, United States
  • USF Health Morsani College of Medicine Department of Neurology Tampa, Florida, United States
  • Children's Hospital of Philadelphia - Buerger Center for Advanced Pediatric Care - PIN Philadelphia, Pennsylvania, United States
View all 34 locations
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Recruiting

A Study to Investigate the Safety, Pharmacokinetics, and Preliminary Efficacy of IDE574 Therapy in Adult Participants With Advanced Solid Tumors

NCT07540572

Conditions
Brain Diseases, Bronchial Neoplasms, Carcinoma, Bronchogenic, +30 more
Locations
  • Florida Clinical Trials Group Plantation, Florida, United States
  • START Astera, LLC East Brunswick, New Jersey, United States
  • START New York Long Island, LLC Lake Success, New York, United States
  • NEXT Texas LLC - Austin Austin, Texas, United States
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Recruiting

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

NCT05224778

Conditions
CDM, Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
Locations
  • University of California, Los Angeles Los Angeles, California, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
  • University of Rochester Medical Center Rochester, New York, United States
  • Virginia Commonwealth University Richmond, Virginia, United States
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Recruiting

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

NCT03981575

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
Locations
  • University of California, San Diego La Jolla, California, United States
  • University of California, Los Angeles Los Angeles, California, United States
  • University of Colorado - Denver Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
View all 17 locations
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Recruiting

A Study to Evaluate the Feasibility of a Physiologic Biomarker to Assess Pain and Other Sensory Problems Using Pupillometry in Participants With Neurofibromatosis Type 1 (NF1)

NCT06507748

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +21 more
Locations
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
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Recruiting

Clinical Course Of Disease In Participants With FA-CM

NCT06865482

Conditions
Brain Diseases, Cardiomyopathies, Cardiomyopathy, +15 more
Locations
  • University of California San Diego La Jolla, California, United States
  • University of South Florida Tampa, Florida, United States
  • Indiana University - Riley Children's Health Indianapolis, Indiana, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
View all 19 locations
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Recruiting

PrP-targeting siRNA Safety & Mechanism Study

NCT07444580

Conditions
Brain Diseases, Central Nervous System Diseases, Central Nervous System Infections, +18 more
Locations
  • Massachusetts General Hospital Boston, Massachusetts, United States
  • Mayo Clinic Rochester, Minnesota, United States
  • Columbia University Medical Center New York, United States
  • University Hospitals Cleveland Medical Center Cleveland, Ohio, United States
View Trial Details

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