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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

Pharmacokinetics, Safety and Efficacy of the Selumetinib Granule Formulation in Children Aged ≥1 to <7 Years With NF1-related Symptomatic, Inoperable PN

NCT05309668

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +14 more
Locations
  • Research Site Akron, Ohio, United States
  • Research Site Philadelphia, Pennsylvania, United States
  • Research Site Houston, Texas, United States
  • Research Site Richmond, Virginia, United States
View all 16 locations
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Active, Not Recruiting

A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)

NCT04573023

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Minnesota Minneapolis, Minnesota, United States
View all 25 locations
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Active, Not Recruiting

Tuvusertib Combined With Niraparib or Lartesertib in Participants With Epithelial Ovarian Cancer (DDRiver EOC 302)

NCT06433219

Conditions
Adnexal Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +24 more
Locations
  • University of Arkansas for Medical Sciences Little Rock, Arkansas, United States
  • University of California San Francisco - UCSF Medical Center San Francisco, California, United States
  • Centricity Research Cancer Center - DBA CRRI John B. Amos Cancer Center Research Columbus, Georgia, United States
  • University of Chicago Comprehensive Cancer Center at Silver Cross - Carolyn J. Czerkies Pavilion Chicago, Illinois, United States
View all 84 locations
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Active, Not Recruiting

Epidyolex® in Lennox Gastaut, Dravet Syndrome and Tuberous Sclerosis Complex: an Observational Study in ITALY

NCT05485831

Conditions
Brain Diseases, Central Nervous System Diseases, Congenital Abnormalities, +25 more
Locations
  • Policlinico Sant'Orsola di Bologna Bologna, Italy
  • NPI AOU Mater Domini Università Magna Graecia Catanzaro, Italy
  • Università degli studi "G. D'annunzio" Chieti Chieti, Italy
  • Azienda Ospedaliera Universitaria Meyer Neurologia Pediatrica Florence, Italy
View all 18 locations
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Active, Not Recruiting

NF-1, Nutraceutical Intervention

NCT05363267

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +13 more
Locations
  • Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
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Active, Not Recruiting

Tuvusertib (M1774) in Combination With Cemiplimab in Participants With Non-Squamous NSCLC (DDRiver NSCLC 322)

NCT05882734

Conditions
Bronchial Neoplasms, Carcinoma, Bronchogenic, Carcinoma, Non-Small-Cell Lung, +19 more
Locations
  • UCLA Hematology and Oncology - Santa Monica Santa Monica, California, United States
  • UPMC Cancer Center Pittsburgh, Pennsylvania, United States
  • Tennessee Cancer Specialists - Biomedical Research Knoxville, Tennessee, United States
  • The University of Texas MD Anderson Cancer Center Houston, Texas, United States
View all 54 locations
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Active, Not Recruiting

Open Label Extension to Assess the Long-Term Safety and Tolerability of ZYN002 in Children and Adolescents With FXS

NCT03802799

Conditions
Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Southwest Autism Research and Resource Center Phoenix, Arizona, United States
  • Science 37 Culver City, California, United States
  • Amnova Clinical Research, LLC Irvine, California, United States
  • UC Davis Health System, MIND Institute Sacramento, California, United States
View all 26 locations
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