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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

A Study of the Drugs Selumetinib Versus Carboplatin/Vincristine in Patients With Neurofibromatosis and Low-Grade Glioma

NCT03871257

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +16 more
Locations
  • Children's Hospital of Alabama Birmingham, Alabama, United States
  • Banner Children's at Desert Mesa, Arizona, United States
  • Phoenix Childrens Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
View all 132 locations
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Active, Not Recruiting

A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease

NCT04884815

Conditions
Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Stanford University Redwood City, California, United States
  • University of California Davis Sacramento, California, United States
  • Northwestern University Chicago, Illinois, United States
View all 16 locations
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Active, Not Recruiting

Phenotype, Genotype and Biomarkers 2

NCT04875416

Conditions
Amyotrophic Lateral Sclerosis, Brain Diseases, Central Nervous System Diseases, +27 more
Locations
  • University of Miami Miami, Florida, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • University of Pennsylvania Philadelphia, Pennsylvania, United States
  • University of Cape Town Cape Town, South Africa
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Active, Not Recruiting

Phenotype, Genotype & Biomarkers in ALS and Related Disorders

NCT02327845

Conditions
Amyotrophic Lateral Sclerosis, Brain Diseases, Central Nervous System Diseases, +28 more
Locations
  • Stanford University Palo Alto, California, United States
  • University of California San Diego (UCSD) San Diego, California, United States
  • California Pacific Medical Center (CPMC) San Francisco, California, United States
  • University of Miami Miami, Florida, United States
View all 15 locations
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Active, Not Recruiting

A Phase IV Study of Safety and Efficacy of Everolimus in Taiwanese Patients With Tuberous Sclerosis Complex Who Have Renal Angiomyolipoma (TSC-AML)

NCT05252585

Conditions
Angiomyolipoma, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +18 more
Locations
  • Novartis Investigative Site Taichung, Taiwan ROC, Taiwan
  • Novartis Investigative Site Taoyuan, Taiwan ROC, Taiwan
  • Novartis Investigative Site Taipei, Taiwan
  • Novartis Investigative Site Taoyuan, Taiwan
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Active, Not Recruiting

A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome

NCT05898620

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +12 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Nicklaus Children's Hospital Research Institute Miami, Florida, United States
View all 16 locations
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