- Conditions
- ATTR Amyloidosis, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +16 more
- Locations
-
- Clinical Trial SIte Paris, France
- Clinical Trial SIte Münster, Germany
- Clinical Trial SIte Porto, Portugal
- Clinical Trial SIte Majorca, Spain
Clinical trial condition
Heredodegenerative Disorders, Nervous System
Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.
1,879 public trials
409 recruiting studies
Heredodegenerative Disorders, Nervous System trial results
Completed
Idebenone to Treat Friedreich's Ataxia
NCT00229632
- Conditions
- Ataxia, Brain Diseases, Central Nervous System Diseases, +16 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT01495260
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
-
- Hospital Universitari de Bellvitge L'Hospitalet de Llobregat, Barcelona, Spain
- Conditions
- Batten Disease, CLN2 Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
- University Hamburg-Eppendorf Hamburg, Germany
- Bambino Gesù Children's Hospital Rome, Italy
- Guy's & St. Thomas NHS Foundation Trust London, United Kingdom
NCT02465931
- Conditions
- Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
-
- RTI International Research Triangle Park, North Carolina, United States
NCT00552955
- Conditions
- Ascites, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +27 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
Completed
Study of Ranolazine in Myotonia Congenita, Paramyotonia Congenita and Myotonic Dystrophy Type 1
NCT02251457
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +12 more
- Locations
-
- The Ohio State University Wexner Medical Center Columbus, Ohio, United States
NCT00667836
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +14 more
- Locations
-
- Shriners Hospitals for Children, Salt Lake City Salt Lake City, Utah, United States
NCT00303368
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +15 more
- Locations
-
- Shriners Hospitals for Children, Intermountain Hospital Salt Lake City, Utah, United States
NCT03848442
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
-
- Center for Rett syndrome, Department of Paediatrics and Adolescents Medicine Copenhagen, København Ø, Denmark