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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,879 public trials 409 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Completed

A Safety and Dose Ranging Study of Idursulfase (Intrathecal) Administration Via an Intrathecal Drug Delivery Device in Pediatric Patients With Hunter Syndrome Who Have Central Nervous System Involvement and Are Receiving Treatment With Elaprase®

NCT00920647

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
Locations
  • University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
  • Birmingham Children's Hospital Birmingham, United Kingdom
  • Birmingham Children's Hospital NHS Foundation Trust Birmingham, United Kingdom
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Completed

Safety, Tolerability, and Efficacy of NBI-98854 for the Treatment of Pediatric Subjects With Tourette Syndrome

NCT03325010

Conditions
Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +10 more
Locations
  • Neurocrine Clinical Site Sun City, Arizona, United States
  • Neurocrine Clinical Site Rogers, Arkansas, United States
  • Neurocrine Clinical Site Anaheim, California, United States
  • Neurocrine Clinical Site San Diego, California, United States
View all 35 locations
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Completed

Safety, Tolerability and Pharmacokinetics of ERX-963 in Adults With Myotonic Dystrophy Type 1

NCT03959189

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disorders of Excessive Somnolence, Dyssomnias, +15 more
Locations
  • Stanford Neurosciences Health Center Palo Alto, California, United States
  • Sleep Medicine Specialists of South Florida Miami, Florida, United States
  • University of Iowa Iowa City, Iowa, United States
  • The Center for Sleep & Wake Disorders Chevy Chase, Maryland, United States
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Completed

Screening Study to Identify Pediatric Patients With Hunter Syndrome Who Demonstrate Evidence of Central Nervous System (CNS) Involvement and Who Are Currently Receiving Treatment With Elaprase®

NCT00937794

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
  • Birmingham Children's Hospital Birmingham, United Kingdom
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Completed

Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich Ataxia

NCT03214588

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +11 more
Locations
  • UCLA Ataxia Center Los Angeles, California, United States
  • University of Florida Center for Movement Disorders Gainesville, Florida, United States
  • USF College of Medicine Tampa, Florida, United States
  • University of Iowa Children's Hospital Iowa City, Iowa, United States
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