Skip to main content
OpenTrials

Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,242 public trials 227 recruiting studies
Refine in advanced search Browse all conditions

Genetic Diseases, X-Linked trial results

Recruiting

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44

NCT07037862

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • University Hospital Gent Ghent, Belgium
  • UZ Leuven Leuven, Belgium
  • Centre Hospitalier Régional de la Citadelle Liège, Belgium
  • IRCCS Ospedale San Raffaele Milan, Italy
View all 14 locations
View Trial Details
Recruiting

NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

NCT05996003

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy, +10 more
Locations
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Rare Disease Research, LLC - FL Kissimmee, Florida, United States
  • Rare Disease Research Atlanta, Georgia, United States
  • Ann and Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 25 locations
View Trial Details
Recruiting

Trial of Cell Based Therapy for DMD

NCT06692426

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Masonic Cancer Center Minneapolis, Minnesota, United States
View Trial Details
Recruiting

Prevalence of Antibodies and Cytokines in Participants With Chronic Granulomatous Disease

NCT06605378

Conditions
Chronic Disease, Chronic Granulomatous Disease (CGD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
Locations
  • Home-based telemedicine Montgomery, Alabama, United States
  • Home-based telemedicine Phoenix, Arizona, United States
  • Home-based telemedicine Little Rock, Arkansas, United States
  • Home-based telemedicine Sacramento, California, United States
View all 52 locations
View Trial Details
Recruiting

RAre, But Not aLone: a Large Italian Network to Empower the Impervious diaGNostic Pathway of Rare cerEbrovascular Diseases (ALIGNED)

NCT06935578

Conditions
Arterial Occlusive Diseases, Brain Diseases, Brain Diseases, Metabolic, +46 more
Locations
  • Ospedale Regionale Generale "F. Miulli", Acquaviva delle Fonti Acquaviva delle Fonti, BA, Italy
  • ASST Melegnano Martesana Melegnano, MI, Italy
  • Neurologia Stroke Unit dell'Asst Rhodense Rho, Mi, Italy
  • Fondazione Istituto G. Giglio, Cefalù Cefalù, PA, Italy
View all 17 locations
View Trial Details
Recruiting

An Observational Cohort Study to Characterize the Effectiveness and Safety of HEMGENIX® in Patients With Hemophilia B

NCT06008938

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • American Thrombosis and Hemostasis Network Rochester, New York, United States
  • Medical University Vienna Vienna, Austria
  • Aarhus Universitetshospital Århus N, Denmark
  • Centre Hospitalier Universitaire de Brest / CHU Morvan Brest, France
View Trial Details

Related conditions