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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,672 public trials 2,143 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

Efficacy and Safety of BIIB111 for the Treatment of Choroideremia

NCT03496012

Conditions
Choroid Diseases, Choroideremia, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +5 more
Locations
  • Research Site Los Angeles, California, United States
  • Research Site Miami, Florida, United States
  • Research Site Baltimore, Maryland, United States
  • Research Site New York, United States
View all 18 locations
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Completed

Bleeding Incidence in VWD Patients Undergoing On-Demand Treatment

NCT04053699

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Blood Platelet Disorders, +8 more
Locations
  • Children's Healthcare of Atlanta Atlanta, Georgia, United States
  • Republican Research Center for Radiation Medicine and Human Ecology Homyel, Belarus
  • Specialized Hospital for Active Treatment of Haematological Diseases" EAD, Sofia Sofia, Bulgaria
  • "UMHAT Sveta Marina" EAD. Varna, Bulgaria
View all 15 locations
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Completed

The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Participants Who Have Already Been Treated With ALN-TTR02 (Patisiran)

NCT02510261

Conditions
Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +12 more
Locations
  • Clinical Trial Site La Mesa, California, United States
  • Clinical Trial Site Aurora, Colorado, United States
  • Clinical Trial Site Jacksonville, Florida, United States
  • Clinical Trial Site Chicago, Illinois, United States
View all 56 locations
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