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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,668 public trials 2,145 recruiting studies
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Genetic Diseases, Inborn trial results

Terminated

Long Term Follow-up (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

NCT04628871

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Carbohydrate Metabolism, Inborn Errors, +24 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • New York University Grossman School of Medicine New York, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
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Terminated

Phase III, Efficacy and Safety of "Kamada-AAT for Inhalation"

NCT04204252

Conditions
Alpha 1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
Locations
  • University Hospital (UZ) Leuven Leuven, Belgium
  • Tays Central Hospital Tampere, Finland
  • Beaumont Hospital Dublin, Ireland
  • Leiden University Medical Center (LUMC) Leiden, ZA, Netherlands
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Withdrawn

Treatment Patterns, Biochemical Profiles and Clinical Outcomes in Adults With X-Linked Hypophosphatemia

NCT07607600

Conditions
Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +26 more
Locations
  • Yale University School of Medicine New Haven, Connecticut, United States
  • Indiana University Hospital Indianapolis, Indiana, United States
  • The Ohio State University Wexner Medical Center (OSUWMC) - CarePoint East Columbus, Ohio, United States
  • Vanderbilt University Medical Center Nashville, Tennessee, United States
View all 23 locations
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