Genetic Diseases, Inborn

• UCSF Benioff Children's Hospital Oakland — Oakland, California, United States
• Ann & Robert H. Lurie Children's Hospital of Chicago — Chicago, Illinois, United States
• New York University Grossman School of Medicine — New York, United States
• University of North Carolina — Chapel Hill, North Carolina, United States

• University Hospital (UZ) Leuven — Leuven, Belgium
• Tays Central Hospital — Tampere, Finland
• Beaumont Hospital — Dublin, Ireland
• Leiden University Medical Center (LUMC) — Leiden, ZA, Netherlands

• National Institutes of Health Clinical Center — Bethesda, Maryland, United States

• Kaiser Permanente — Los Angeles, California, United States
• Columbia University — New York, United States
• UPMC Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania, United States
• Lysosomal and Rare Disorders Research and Treatment Center — Fairfax, Virginia, United States

• Washington University School of Medicine — St Louis, Missouri, United States

Not specified

Not specified