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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,672 public trials 2,143 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Study to Assess the Safety, Tolerability, and Efficacy of ST-400 for Treatment of Transfusion-Dependent Beta-thalassemia (TDT)

NCT03432364

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
Locations
  • University of California, Los Angeles Los Angeles, California, United States
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Children's Healthcare of Atlanta Atlanta, Georgia, United States
  • Dana-Farber Boston Children's Cancer and Blood Disorders Center Boston, Massachusetts, United States
View Trial Details
Completed

iCanCope With Sickle Cell Pain

NCT03201874

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
Locations
  • Connecticut Children's Medical Center Hartford, Connecticut, United States
  • Emory University Atlanta, Georgia, United States
  • Seattle Children's Hospital Seattle, Washington, United States
  • The Hospital for Sick Children Toronto, Ontario, Canada
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Completed

An Open Label Study to Determine the Safety and Efficacy of Recombinant Human Coagulation Factor VIII-Fc Fusion Protein for Injection in Adolescent and Adult Patients With Hemophilia A.

NCT04456387

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
Locations
  • Anhui Provincial Hospital Hefei, Anhui, China
  • Capital Medical University affiliated Beijing Children's Hospital Beijing, Beijing Municipality, China
  • Chongqing Three Gorges Central Hospital Chongqing, Chongqing Municipality, China
  • Fujian Medical University Union Hospital Fuzhou, Fujian, China
View all 17 locations
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