- Conditions
- Anderson-Fabry Disease, Aortic Stenosis, Subvalvular, Aortic Valve Disease, +67 more
- Locations
-
- IRCCS San Raffaele Scientific Institute Milan, Milano, Italy
Clinical trial condition
Fabry Disease
Explore clinical trials studying Fabry Disease. Study availability and eligibility vary by location and protocol.
177 public trials
37 recruiting studies
Fabry Disease trial results
Recruiting
Evaluate the Safety and Efficacy of Fabagal® (Agalsidase Beta) in Patients With Fabry Disease
NCT06081062
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Philippine General Hospital Manila, Philippines
- St.Luke's Medical Center Manila, Philippines
- Seoul Asan Center Seoul, Songpa-gu, South Korea
NCT06207552
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Children's Hospital of Fudan University Shanghai, China
NCT00455104
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Alberta Children's Hospital Calgary, Alberta, Canada
- Vancouver General Hospital Adult Metabolic Diseases Clinic Vancouver, British Columbia, Canada
- Queen Elizabeth II Health Sciences Centre Halifax, Nova Scotia, Canada
- Toronto Western Hospital Toronto, Ontario, Canada
Recruiting
Biomarkers and Cardiac Imaging Diagnostic Assay for Monitoring Patients With Fabry Disease
NCT05698901
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
-
- Charles Jia-Yin Hou Taipei, Taiwan
Recruiting
National Registry of Rare Kidney Diseases
NCT06065852
- Conditions
- AH Amyloidosis, AHL Amyloidosis, AL Amyloidosis, +207 more
- Locations
-
- Zoe Plummer Bristol, South West, United Kingdom
NCT03362164
- Conditions
- Aortic Stenosis, Subvalvular, Aortic Valve Disease, Aortic Valve Stenosis, +43 more
- Locations
-
- Wuerzburg University Hospital Würzburg, Bavaria, Germany
Not yet recruiting
A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease
NCT07778667
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
Not specified
Not yet recruiting
Care Pathway for Patients With Fabry's Disease (Fabry-PATH)
NCT07485660
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Service de Cardiologie - 1 Avenue du Professeur Jean Poulhès Toulouse, Occitanie, France
Not yet recruiting
Novel Diagnostic and Prognostic Predictors in Fabry Cardiomyopathy: Proof of Concept in a Rare Disease
NCT07351136
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
Not specified
Related conditions
- Brain Diseases (177)
- Brain Diseases, Metabolic, Inborn (177)
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (177)
- Genetic Diseases, X-Linked (177)
- Lipid Metabolism, Inborn Errors (177)
- Lysosomal Storage Diseases, Nervous System (177)
- Metabolism, Inborn Errors (177)
- Nutritional and Metabolic Diseases (177)