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Clinical trial condition

Wolman Disease

Explore clinical trials studying Wolman Disease. Study availability and eligibility vary by location and protocol.

19 public trials 2 recruiting studies

Wolman Disease trial results

Conditions
Cholesterol Ester Storage Disease, Cholesterol Ester Storage Disease(CESD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
Locations
  • Stanford, California, United States
  • New York, United States
  • Pittsburgh, Pennsylvania, United States
  • Prague, Czechia
Conditions
Cholesterol Ester Storage Disease, Cholesterol Ester Storage Disease (CESD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
Locations
  • Eureka, California, United States
  • Sacramento, California, United States
  • San Francisco, California, United States
  • Minneapolis, Minnesota, United States
Conditions
Cholesterol Ester Storage Disease, Cholesterol Ester Storage Disease(CESD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
Locations
  • Stanford University Stanford, California, United States
  • Children's Memorial Hospital Chicago, Illinois, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Morgan Stanley Children's Hospital of New York-Presbyterian New York, United States
View all 16 locations
Conditions
Cholesterol Ester Storage Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
Locations
  • Cedars-Siani Medical Center Los Angeles, California, United States
  • Stanford University Palo Alto, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Columbia University New York, United States
View all 14 locations

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States