Completed
Study of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type Ia
NCT03970278
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- UCONN Health Farmington, Connecticut, United States
- Michigan Medicine University of Michigan Ann Arbor, Michigan, United States
- University of Texas Health Science Center at Houston Houston, Texas, United States
- Montreal Children Hospital, McGill University Health Centre Montreal, Quebec, Canada