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Clinical trial condition

Hepatorenal form of glycogen storage disease

Explore clinical trials studying Hepatorenal form of glycogen storage disease. Study availability and eligibility vary by location and protocol.

10 public trials 4 recruiting studies
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Hepatorenal form of glycogen storage disease trial results

Recruiting

Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program

NCT06636383

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
Locations
  • Children's Hospital of Orange County Orange, California, United States
  • Children's Hospital Colorado Denver, Colorado, United States
  • University of Connecticut Health Center Hartford, Connecticut, United States
  • University of Michigan Ann Arbor, Michigan, United States
View all 19 locations
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Completed

A Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia (GSDIa)

NCT05139316

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
Locations
  • Children's Hospital of Orange County Orange, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • University of Connecticut Health Center Farmington, Connecticut, United States
  • Mount Sinai The Bronx, New York, United States
View all 20 locations
View Trial Details
Completed

Study of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type Ia

NCT03970278

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
Locations
  • UCONN Health Farmington, Connecticut, United States
  • Michigan Medicine University of Michigan Ann Arbor, Michigan, United States
  • University of Texas Health Science Center at Houston Houston, Texas, United States
  • Montreal Children Hospital, McGill University Health Centre Montreal, Quebec, Canada
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