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Clinical trial condition

Sphingolipidoses

Explore clinical trials studying Sphingolipidoses. Study availability and eligibility vary by location and protocol.

390 public trials 81 recruiting studies
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Sphingolipidoses trial results

Completed

Study to Evaluate Efficacy and Safety of Imiglucerase Treatment in Chinese Patients With Gaucher Disease Type Ⅲ

NCT04656600

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Investigational Site Number : 107 Beijing, China
  • Investigational Site Number : 101 Beijing, China
  • Investigational Site Number : 104 Chengdu, China
  • Investigational Site Number : 102 Guangzhou, China
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Completed

China Post-marketing Surveillance (PMS) Study of Fabrazyme®

NCT05054387

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Investigational Site Number :1560003 Beijing, China
  • Investigational Site Number :1560002 Beijing, China
  • Investigational Site Number :1560001 Shanghai, China
  • Investigational Site Number :1560004 Shanghai, China
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Completed

Baby Detect : Genomic Newborn Screening

NCT05687474

Conditions
3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
Locations
  • CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
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Completed

A Study of Velaglucerase Alfa (VPRIV) in Chinese Children, Teenagers, and Adults With Type 1 Gaucher Disease

NCT05529992

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Chinese PLA General Hospital Beijing, Beijing Municipality, China
  • Beijing Children's Hospital, Capital Medical University Beijing, Beijing Municipality, China
  • Peking Union Medical College Hospital, Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Lanzhou University Second Hospital Lanzhou, Gansu, China
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