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Clinical trial condition

Severe Combined Immunodeficiency, X Linked

Explore clinical trials studying Severe Combined Immunodeficiency, X Linked. Study availability and eligibility vary by location and protocol.

2 public trials 1 recruiting study

Severe Combined Immunodeficiency, X Linked trial results

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gene Therapy, Genetic Diseases, Inborn, +8 more
Locations
  • Mattel Children's Hospital - UCLA Los Angeles, California, United States
  • Emory University/Childrens Healthcare of Atlanta Atlanta, Georgia, United States
  • Boston Childrens Hospital Boston, Massachusetts, United States
  • Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States