NCT03311503
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gene Therapy, Genetic Diseases, Inborn, +8 more
- Locations
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- Mattel Children's Hospital - UCLA Los Angeles, California, United States
- Emory University/Childrens Healthcare of Atlanta Atlanta, Georgia, United States
- Boston Childrens Hospital Boston, Massachusetts, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States