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OpenTrials

Clinical trial condition

Rare Diseases

Explore clinical trials studying Rare Diseases. Study availability and eligibility vary by location and protocol.

466 public trials 83 recruiting studies

Rare Diseases trial results

Conditions
Autoimmune Diseases, Autoimmune Diseases of the Nervous System, Autoimmune Encephalitis, +10 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • St. Joseph Hospital and Medical Center Barrow Neurological Institute Phoenix, Arizona, United States
  • Mayo Clinic in Arizona Scottsdale, Arizona, United States
  • Children's Hospital of Orange County Orange, California, United States
View all 39 locations

NCT04220190

Conditions
Amyotrophic Lateral Sclerosis, Central Nervous System Diseases, Disease Attributes, +12 more
Locations
  • Massachusetts General Hospital Boston, Massachusetts, United States
Conditions
Ataxia, Brain Diseases, Central Nervous System Diseases, +19 more
Locations
  • UCLA Ataxia Center Los Angeles, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida - Neurology Gainesville, Florida, United States
  • USF Ataxia Research Center Tampa, Florida, United States
View all 34 locations

NCT06969209

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +14 more
Locations
  • University Hospital Inselspital, Department of Diabetes, Endocrinology, Nutritional Medicine and Metabolism (UDEM) Bern, Switzerland