Skip to main content
OpenTrials

Clinical trial condition

Rare Diseases

Explore clinical trials studying Rare Diseases. Study availability and eligibility vary by location and protocol.

473 public trials 86 recruiting studies
Refine in advanced search Browse all conditions

Rare Diseases trial results

Recruiting

Real-World Effectiveness and Safety of Pegcetacoplan in Patients With C3G or IC-MPG: A Multi-Country Study

NCT07746895

Conditions
C3 Glomerulopathy (C3G), Disease Attributes, Female Urogenital Diseases, +11 more
Locations
  • Nepean Hospital Kingswood, Australia
  • Princess Alexandra Hospital Woolloongabba, Australia
  • Medizinische Universität Graz Graz, Austria
  • Uniklinik Innsbruck Innsbruck, Austria
View all 101 locations
View Trial Details
Recruiting

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

NCT06016946

Conditions
Ataxia, Brain Diseases, Central Nervous System Diseases, +19 more
Locations
  • UCLA Ataxia Center Los Angeles, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida - Neurology Gainesville, Florida, United States
  • USF Ataxia Research Center Tampa, Florida, United States
View all 34 locations
View Trial Details
Recruiting

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

NCT07180355

Conditions
Ataxia, Brain Diseases, Central Nervous System Diseases, +21 more
Locations
  • The University of California, Los Angeles (UCLA) Los Angeles, California, United States
  • The Ohio State University Columbus, Ohio, United States
  • The Children's Hospital of Philadelphia (CHOP) Philadelphia, Pennsylvania, United States
View Trial Details
Recruiting

International Rare Brain Tumor Registry

NCT05697874

Conditions
Astroblastoma, BCOR ITD Sarcoma, CNS Sarcoma, +12 more
Locations
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • University of California San Francisco San Francisco, California, United States
  • Children's National Hospital Washington D.C., District of Columbia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 13 locations
View Trial Details
Recruiting

Education & Care in RARE: Efficacy of Targeted Psychoeducational Intervention Among Pediatric Rare Disease Patients

NCT06729554

Conditions
Disease Attributes, Inborn Errors of Metabolism Disorders, Orphan Diseases, +5 more
Locations
  • Medical University of Graz Graz, Austria
  • Medical University of Innsbruck Innsbruck, Austria
  • The Faculty of Medicine JKU Linz Linz, Austria
  • SALK PMU Salzburg, Austria
View Trial Details

Related conditions