Skip to main content

Find Clinical Trials

Home
Conditions
Rare Diseases

Clinical trial condition

Rare Diseases

Explore clinical trials studying Rare Diseases. Study availability and eligibility vary by location and protocol.

467 public trials 83 recruiting studies

Refine in advanced search Browse all conditions

Rare Diseases trial results

Completed

Phase III Randomized Study of Poloxamer 188 for Vaso-Occlusive Crisis of Sickle Cell Disease

NCT00004408

Conditions: Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +14 more
Locations: Not specified

View Trial Details

Completed

Clinical and Molecular Correlations in Spinocerebellar Ataxia Type 10 (SCA10)

NCT00004306

Conditions: Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +15 more
Locations: University of Texas Medical Branch at Galveston Galveston, Texas, United States

View Trial Details

Completed

Absorption of Corticosteroids in Children With Juvenile Dermatomyositis

NCT00004357

Conditions: Cardiovascular Diseases, Connective Tissue Diseases, Dermatomyositis, +22 more
Locations: Children's Memorial Hospital, Chicago Chicago, Illinois, United States

View Trial Details

Completed

Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C

NCT01344798

Conditions: Disease Attributes, Gamma-sarcoglycanopathy, Limb Girdle Muscular Dystrophy Type 2C, +6 more
Locations: Hôpital Pitié-Salpêtrière Paris, France

View Trial Details

Completed

Phase I Study of Liposome-Mediated Gene Transfer in Patients With Cystic Fibrosis

NCT00004806

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Digestive System Diseases, +9 more
Locations: Not specified

View Trial Details

Completed

Phase I Pilot Study of Gene Therapy for Cystic Fibrosis Using Cationic Liposome Mediated Gene Transfer

NCT00004471

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Digestive System Diseases, +9 more
Locations: Not specified

View Trial Details

Completed

Phase II Study of Alendronate Sodium in Children With High-Turnover Idiopathic Juvenile Osteoporosis

NCT00010439

Conditions: Arthritis, Bone Diseases, Bone Diseases, Metabolic, +12 more
Locations: Medical University of South Carolina Charleston, South Carolina, United States

View Trial Details

Completed

Phase II Randomized Study of Muromonab-CD3, Cyclosporine, Methylprednisolone, and Prednisone in Patients With Giant Cell Myocarditis

NCT00004482

Conditions: Cardiomyopathies, Cardiovascular Diseases, Disease Attributes, +7 more
Locations: Mayo Clinic Rochester, Minnesota, United States

View Trial Details

Completed

Study of Hepatic Glucose Production and De Novo Lipogenesis in Patients With Cystic Fibrosis

NCT00014781

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Digestive System Diseases, +9 more
Locations: Southwest Medical Center at Dallas Dallas, Texas, United States

View Trial Details

Completed

Study of Magnesium Sulfate in Children With Reduced Bone Density Secondary to Chronic Cholestatic Liver Disease

NCT00007033

Conditions: Abnormalities, Multiple, Alagille Syndrome, Bile Duct Diseases, +18 more
Locations: Children's Hospital Medical Center - Cincinnati Cincinnati, Ohio, United States

View Trial Details