Skip to main content
OpenTrials

Clinical trial condition

Rare Diseases

Explore clinical trials studying Rare Diseases. Study availability and eligibility vary by location and protocol.

467 public trials 83 recruiting studies

Rare Diseases trial results

Conditions
Autoimmune Diseases, Autoimmune Diseases of the Nervous System, Chronic Disease, +13 more
Locations
  • CHU de Bordeaux - Hôpital Pellegrin Bordeaux, France
  • Hôpital général du CHU de Dijon Dijon, France
  • CHU de Nice - Hôpital l'Archet Nice, France
  • CHU Paris - Hôpital Pitié salpétrière Paris, France
View all 33 locations
Conditions
Anemia, Anemia, Hemolytic, Bone Marrow Diseases, +9 more
Locations
  • State budgetary healthcare institution "Chelyabinsk Regional Clinical Hospital" Chelyabinsk, Chelyabinsk Oblast, Russia
  • Federal State Budgetary Institution of Science "Kirov Research Institute of Hematology and Blood Transfusion of the Federal Medical and Biological Agency" Kirov, Kirov Oblast, Russia
  • Federal State Budgetary Educational Institution of Higher Education "First St. Petersburg State Medical University named after Academician I.P. Pavlov" Saint Petersburg, Leningradskaya Oblast', Russia
  • Federal State Budgetary Institution "National Medical Research Center of Hematology" of the Ministry of Health of the Russian Federation Moscow, Moscow Oblast, Russia
Conditions
Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, +1 more
Locations
  • Rady's/Children's Hospital of Orange County Orange, California, United States
  • Washington University in St. Louis School of Medicine & St. Louis Children's Hospital St Louis, Missouri, United States
  • University of Nebraska Medical Center & Children's Hospital Omaha, Nebraska, United States
  • Children's Hospital of Philadelpia Philadelphia, Pennsylvania, United States
Conditions
Central Nervous System Diseases, Disease Attributes, Mental Disorders, +13 more
Locations
  • Craig Hospital Englewood, Colorado, United States
  • Shepherd Center Atlanta, Georgia, United States
  • University Hospital Of Cleveland Cleveland, Ohio, United States
  • The Methodist Hospital Houston, Texas, United States
Conditions
Alpha Mannosidosis, Bone Diseases, Bone Diseases, Developmental, +15 more
Locations
  • Department of Pediatrics, Charles University Prague, Czechia
  • University of Mainz Mainz, Germany
  • Department of Medicine, University of Tromsoe Tromsø, Norway
  • Willink Biochemical Genetics Unit,. Royal Manchester Children's Hospital Manchester, United Kingdom
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Baylor College of Medicine Houston, Texas, United States
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Miami Children's Hospital Miami, Florida, United States
  • University of Minnesota Minneapolis, Minnesota, United States
Conditions
Disease Attributes, Hemic and Lymphatic Diseases, Immune System Diseases, +11 more
Locations
  • Northwestern University Feinberg School of Medicine - Department of Hematology/Oncology Chicago, Illinois, United States
  • University of Nebraska Medical Center Omaha, Nebraska, United States
  • MD Anderson Cancer Center Houston, Texas, United States
  • Academia Nacional de Medicina - Oncohematology Department, Instituto de Investigaciones Hematologicas Buenos Aires, Argentina
View all 51 locations
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations
  • Children's National Health System Washington D.C., District of Columbia, United States
  • New York University Langone Medical Center New York, United States
  • University of Utah Hospital Salt Lake City, Utah, United States
  • Centro Hospitalar do Porto Porto, Portugal