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OpenTrials

Clinical trial condition

Pompe Disease

Explore clinical trials studying Pompe Disease. Study availability and eligibility vary by location and protocol.

54 public trials 9 recruiting studies

Pompe Disease trial results

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • Tower Hematology/Oncology Medical Group Beverly Hills, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • Washington University Medical Center St Louis, Missouri, United States
  • Mount Sinai School of Medicine New York, United States
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Birmingham, Alabama, United States
  • Stanford, California, United States
  • Washington D.C., District of Columbia, United States
  • Chicago, Illinois, United States
Conditions
Acid Maltase Deficiency Disease, Brain Diseases, Brain Diseases, Metabolic, +15 more
Locations
  • University of Florida College of Medicine Gainesville, Florida, United States
  • Duke University Medical Center Durham, North Carolina, United States
  • Children's Hospital Medical Center Cincinnati, Ohio, United States
  • Pediatrique Hopital de Brousse Lyon, France
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • University of Florida Gainesville, Florida, United States
  • Washington University St Louis, Missouri, United States
  • Center for Metabolic Disorders Lake Success, New York, United States
  • Duke University Durham, North Carolina, United States