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OpenTrials

Clinical trial condition

Pompe Disease

Explore clinical trials studying Pompe Disease. Study availability and eligibility vary by location and protocol.

54 public trials 9 recruiting studies
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Pompe Disease trial results

Completed

Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (STIG-Pompe-Study)

NCT02824068

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • Friedrich-Baur-Institute, Dep. of Neurology Klinikum der Universitaet Muenchen Munich, Germany Munich, Bavaria, Germany
  • 5. Department of Clinical and Experimental Medicine, Reference Center for Rare Neuromuscular Disorders, University of Messina, Italy Messina, Sicily, Italy
  • National Taiwan University Hospital Taipei Taipei, Taiwan
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Completed

Pompe Disease QMUS and EIM

NCT02742298

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • Duke University Medical Center Durham, North Carolina, United States
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Completed

Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease

NCT01230801

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • Univ of California San Diego School of Medicine La Jolla, California, United States
  • University of Florida College of Medicine Gainesville, Florida, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • Royal Adelaide Hospital, SA Pathology Adelaide, Adelaide, SA, Australia
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