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Clinical trial condition

Pelizaeus-Merzbacher Disease

Explore clinical trials studying Pelizaeus-Merzbacher Disease. Study availability and eligibility vary by location and protocol.

8 public trials 5 recruiting studies
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Pelizaeus-Merzbacher Disease trial results

Recruiting

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

NCT05659901

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
Locations
  • Ionis Investigative Site Atlanta, Georgia, United States
  • Ionis Investigative Site Philadelphia, Pennsylvania, United States
  • Ionis Investigative Site Clermont-Ferrand, France
  • Ionis Investigative Site Le Kremlin-Bicêtre, France
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Recruiting

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

NCT06150716

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
Locations
  • Ionis Investigative Site Atlanta, Georgia, United States
  • Ionis Investigative Site Philadelphia, Pennsylvania, United States
  • Ionis Investigative Site Salt Lake City, Utah, United States
  • Ionis Investigative Site Le Kremlin-Bicêtre, France
View Trial Details
Recruiting

The Myelin Disorders Biorepository Project

NCT03047369

Conditions
4H Syndrome, ADLD, AGS, +173 more
Locations
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
  • University of California, Davis (UC Davis Health) Sacramento, California, United States
View all 23 locations
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