- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- University Medical Center Hamburg-Eppendorf (UKE)- Childrens Hospital Hamburg, Germany
- Greater Ormond Street Hospital London, United Kingdom
Clinical trial condition
Neuronal Ceroid Lipofuscinosis Type 2
Explore clinical trials studying Neuronal Ceroid Lipofuscinosis Type 2. Study availability and eligibility vary by location and protocol.
2 public trials
1 recruiting study
Neuronal Ceroid Lipofuscinosis Type 2 trial results
Active, Not Recruiting
Intravitreal ERT to Prevent Retinal Disease Progression in Children With CLN2
NCT05152914
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States