NCT02485899
- Conditions
- Batten Disease, CLN2 Disease, CLN2 Disorder, +14 more
- Locations
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- Nationwide Children's Hospital Columbus, Ohio, United States
- Universitaetsklinikum Hamburg-Eppendorf Hamburg, Germany
- Children's Hospital Bambino Gesù,IRCCS Rome, Piazza, Italy
- Great Ormond Street Childrens Hospital London, United Kingdom