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Clinical trial condition

Myotonic Dystrophy

Explore clinical trials studying Myotonic Dystrophy. Study availability and eligibility vary by location and protocol.

107 public trials 36 recruiting studies
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Myotonic Dystrophy trial results

Recruiting

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

NCT07486934

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
Locations
  • UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • IU Health Neuroscience Center Indianapolis, Indiana, United States
  • Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
View all 24 locations
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Recruiting

Personalized Training for People With Rare Neuromuscular Disorders

NCT06708468

Conditions
Charcot Marie Tooth Disease (CMT), Charcot-Marie-Tooth Disease, Congenital Abnormalities, +20 more
Locations
  • Haukeland University Hospital Bergen, Norway
  • Helse Møre and Romsdal HF (Molde Hospital) Molde, Norway
  • Namsos Hospital Namsos, Norway
  • Oslo University Hospital Oslo, Norway
View Trial Details
Recruiting

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

NCT05224778

Conditions
CDM, Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
Locations
  • University of California, Los Angeles Los Angeles, California, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
  • University of Rochester Medical Center Rochester, New York, United States
  • Virginia Commonwealth University Richmond, Virginia, United States
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Recruiting

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

NCT03981575

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
Locations
  • University of California, San Diego La Jolla, California, United States
  • University of California, Los Angeles Los Angeles, California, United States
  • University of Colorado - Denver Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
View all 17 locations
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Recruiting

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

NCT06185764

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +15 more
Locations
  • Stanford Neuromuscular Research San Carlos, California, United States
  • University of Florida Clinical Research Center Gainesville, Florida, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
View all 26 locations
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Recruiting

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

NCT06844214

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +9 more
Locations
  • University of Florida, 2004 Mowry Road - Site Number: 8400005 Gainesville, Florida, United States
  • University of South Florida - Neuromuscular Research, 13330 USF Laurel Drive - Site Number: 8400001 Tampa, Florida, United States
  • Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003 New York, United States
  • Virginia Commonwealth University Medical Center- Site Number : 8400006 Richmond, Virginia, United States
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