NCT02562066
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Myasthenic Syndromes, Congenital, +3 more
- Locations
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- UCLA Department of Neurology Los Angeles, California, United States
- Johns Hopkins Pediatric Neurology Baltimore, Maryland, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Ohio State University Columbus, Ohio, United States