Active, Not Recruiting
Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I)
NCT05775848
- Conditions
- Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I), Muscular Dystrophy, Limb-Girdle, Type 2I
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- University of California Irvine Irvine, California, United States
- University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
- University of Florida Gainsville, Florida, United States